Columnist Helen Baldwin finds the perfect gift for her granddaughter's birthday, one of the many unexpected blessings in her ...

SMA gene therapy Zolgensma safely improved motor function in children with SMA who needed tracheostomy, a real-world study showed.

Columnist Connie Chandler writes about her family's tradition of baking and decorating holiday cookies, a project that SMA ...

Fatigue in the diaphragm may contribute to breathing issues in people with spinal muscular atrophy, a new study reports.

The specialty pharmacy Orsini was selected as a partner to provide Itvisma, the newly approved gene therapy for people with ...

Columnist Connie Chandler gives thanks for the acts of kindness her caregivers perform — the sweet stuff that makes life so ...

The FDA's approval of SMA treatment Itvisma marks an "important moment" for the SMA community, a Novartis executive says.

Columnist Sherry Toh prefers holiday giving rather than receiving and making others happy, because what she wants isn't found in stores.

Spinal muscular atrophy, or SMA, is a genetic disorder that is divided into five main types. Historically, people were categorized based on the age at which symptoms first appear, but now, in the ...

Spinal muscular atrophy (SMA) is a rare genetic condition characterized by progressive muscle weakness and atrophy. It mainly affects motor function, but often also causes problems with speaking, ...

There are several treatment options available for spinal muscular atrophy (SMA), a rare genetic condition characterized by progressive muscle weakness and wasting. The disease mainly affects motor ...