To the research team working to save him, KJ Muldoon was first known only as Patient Eta. But within months, KJ’s name — and ...
This year, gene-editing technology was customized to fix mutations in a single patient’s genes for the first time.
A groundbreaking new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) ...
A cutting-edge base-edited CAR T-cell therapy is opening a revolutionary new frontier for patients battling aggressive T-cell leukemia.
A new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) and Great Ormond ...
Almost two thirds of patients with T-cell acute lymphoblastic leukaemia involved in a clinical trial of the treatment are now ...
On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...
A single-dose gene replacement therapy is found to improve movement ability in children over 2 years of age and teenagers with spinal muscular atrophy, according to research published in Nature ...
New three-year follow-up results from the TRANSCEND FL trial show that patients with relapsed or refractory follicular ...