To the research team working to save him, KJ Muldoon was first known only as Patient Eta. But within months, KJ’s name — and ...
Vertex Pharmaceuticals said on Saturday its gene therapy helped children aged between 5 and 11 years with sickle cell disease ...
The launch of BIRSA 101 marks a major breakthrough in CRISPR gene-editing technology, positioning India to deliver affordable ...
A groundbreaking new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) ...
Casgevy, now a "national priority" drug, helped kids with sickle cell and thalassemia, results which may help toward a label ...
A cutting-edge base-edited CAR T-cell therapy is opening a revolutionary new frontier for patients battling aggressive T-cell leukemia.
To compete at iGEM, a sort of science Olympics, teens at a Georgia high school set their sights on finding a better way to ...
A new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) and Great Ormond ...
Despite a challenging CASGEVY launch, high cash burn, and an almost 10% YTD share count growth, CRISPR’s pipeline breadth and ...
A new FDA pathway could speed bespoke gene therapies, but key questions over scope and commercial viability remain.