Children with rare disorders at risk due to interruptions in treatment: Medical group

The Indian Medical Parliamentarians Forum (IMPF) - a cross-party group of 45 MPs who are also medical professionals -- has sought uninterrupted access to Enzyme Replacement Therapy for children ...

MPs flag stalled rare-disease funding; warn nearly 100 children on life-saving therapy face imminent risk

The Indian Medical Parliamentarians’ Forum (IMPF), a cross-party collective of 45 medical professionals turned ...
Precision Medicine Online

Hunter Syndrome Gene Therapy Improves Key Disease Enzyme in First Treated Patients in UK

Researchers have given the gene therapy made at UManchester to two out of five planned patients in a Phase I/II trial, and ...

Couple struggling to access 'vital' cancer drug

A couple struggling to access to a vital cancer treatment say they are are "extremely stressed" by the uncertainty in its ...

Royalty Pharma and Denali Therapeutics Announce $275 Million Royalty Funding Agreement

Detailed price information for Royalty Pharma Plc Cl A (RPRX-Q) from The Globe and Mail including charting and trades.

Denali Therapeutics and Royalty Pharma Announce $275 Million Royalty Funding Agreement

Detailed price information for Royalty Pharma Plc Cl A (RPRX-Q) from The Globe and Mail including charting and trades.
Zacks Investment Research on MSN

Denali enters into a $275M funding deal with Royalty Pharma

Denali Therapeutics Inc. DNLI has announced a funding agreement with Royalty Pharma plc RPRX for $275 million. The stock ...

Denali makes $275m funding agreement with Royalty Pharma

Denali has entered a $275m royalty funding agreement with Royalty Pharma based on future net sales of tividenofusp alfa ...