UC San Diego scientists discover enzyme responsible for scrambling cancer genomes; results could enable new treatments for ...

A parliamentary forum has urged urgent action on funding shortfalls and treatment delays for patients with Lysosomal Storage ...

The Indian Medical Parliamentarians’ Forum (IMPF), a cross-party collective of 45 medical professionals turned ...

The Indian Medical Parliamentarians Forum (IMPF) — ?a cross-party group of 45 MPs who are also medical professionals — ?has sought uninterrupted access to Enzyme Replacement Therapy for children ...

The Indian Medical Parliamentarians’ Forum (IMPF), a group of 45 members of parliament who are also medical professionals, ...

Researchers have given the gene therapy made at UManchester to two out of five planned patients in a Phase I/II trial, and ...

A couple struggling to access a vital cancer treatment say they are "extremely stressed" by the uncertainty in its supply.

Denali Therapeutics Inc. DNLI has announced a funding agreement with Royalty Pharma plc RPRX for $275 million. The stock ...

The FDA has placed a hold on Denali Therapeutics’ plans to launch a phase 1 rare disease trial, citing concerns about immune ...