The effects allowed these minors who could sit but not stand to move like they've never done before, including walking and ...

Eli Lilly and Company has finalized its acquisition of Adverum Biotechnologies, a move that delivers a promising gene therapy ...

A new wave of gene therapy treatments offer a new lease on life for people with inherited diseases such as haemophilia. But ...

A cutting-edge base-edited CAR T-cell therapy is opening a revolutionary new frontier for patients battling aggressive T-cell leukemia.

Zevaskyn, the first gene therapy for recessive dystrophic epidermolysis bullosa, showed significant wound healing in phase 3 ...

Solid Biosciences Inc. (Nasdaq: SLDB) (the 'Company” or 'Solid”), a life sciences company developing precision genetic ...

Investor optimism has waned as final minutes from uniQure’s pre-BLA meeting with the FDA convey that data from the company’s ...

CAR7, has shown remarkable success in reversing an aggressive form of leukemia. This world-first treatment uses genetically ...

The company will begin filing to global regulators in the first half of 2026. Read more at straitstimes.com. Read more at ...

Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain.

Miltenyi Biotec has been honoured with the Special Recognition Award for Pioneering Work in Cell & Gene Therapy at the ...