Research by University of Sydney scientists has uncovered a mechanism that may explain why glioblastoma returns after ...
A mom was overjoyed when she learned a gene therapy treatment could save her child's life, until she found out no one would ...
A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...
Scientists have identified a small flaw in the enzyme GPX4 that prevents neurons from defending themselves. This mutation, ...
Scientists discovered that certain gene changes allow cells to function even when frataxin, the protein lost in Friedreich’s ...
The FDA on Tuesday approved etuvetidigene autotemcel (Waskyra) as the first cell-based gene therapy for patients 6 months and ...
A new University of California San Diego School of Medicine study offers a unified biological model to explain how genetic ...
The three-hit model, developed from more than a decade of systems biology research, proposes that autism develops when three ...
Kids and teenagers with spinal muscular atrophy had more mobility after receiving a single-dose gene replacement therapy, ...
BBC Breakfast took an emotional turn as Sally Nugent and Jon Kay spoke with Alyssa Tapley ...
Researchers explored this question at ASH and shared data suggesting genomic instability in tumors with high TMB likely ...