The patchwork rollout of a gene therapy exposes weaknesses in the pricing and regulatory frameworks that determine who ...
A South Jersey college student with hemophilia B is now living a more normal life thanks to treatment developed from research ...
Risto-cel, a gene-edited cell therapy formerly called BEAM-101, for severe SCD, benefits patients for nearly two years, new ...
Dr. Teresa Blankmeyer Burke is spending the fall semester in Florianópolis, a city in southern Brazil, to study the ethics of ...
ORLANDO -- A gene therapy that could transform CAR T-cell treatment achieved rapid and potentially durable measurable ...
Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...
The National Academy of Inventors (NAI) today released the list of newly inducted fellows, and two Duke researchers have been ...
Abeona Therapeutics Inc. (Nasdaq: ABEO) today announced activation of The University of Texas Medical Branch (UTMB) in ...
A cutting-edge therapy using base-edited immune cells is offering a major breakthrough for patients with one of the toughest ...
An experimental gene therapy treatment created at UCLA gave a "bubble girl" born with a rare genetic disorder a new life.
From rare diseases to chronic conditions, epigenetic editing unlocks new ways to control gene activity without altering the genetic code.
Renowned molecular biologist Yunsun Nam, Ph.D., Professor in the Departments of Biochemistry and Biophysics and the Doris and ...