This year, gene-editing technology was customized to fix mutations in a single patient’s genes for the first time.
Presented new data in non-human primates (NHP) for sickle cell disease (SCD), where RNA Gene Writer achieved approximately 40% and 60% of long-term hematopoietic stem cells (LT-HSCs) with at least one ...
In the latest research, led by experts at UT Southwestern, biologist Jun Wu identified a mouse cell protein named MAVS, which ...
Following a single subcutaneous 240 mg dose, WVE-007 (INHBE GalNAc-siRNA) improved body composition at three months compared ...