To the research team working to save him, KJ Muldoon was first known only as Patient Eta. But within months, KJ’s name — and ...

This year, gene-editing technology was customized to fix mutations in a single patient’s genes for the first time.

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an effective cure for beta-thalassemia and sickle cell disease in children younger ...

Syntax Bio, a synthetic biology company programming the next generation of cell therapies, has published new research in ...

Biotech startup CrisprBits uses CRISPR-based techniques to change the shape of diagnostics by decoding genetic sequencing ...

A rare disease mom and scientist shares on the "First Opinion Podcast" how she serves as a translator between her two ...

Comparing the genomes of snakes with distinct coloration patterns pinpointed the genetic variants that contribute to these ...

For years, Yale researchers David Breslow and Mustafa Khokha have worked together with a similar challenge in their ...

When UC Berkeley biochemist Jennifer Doudna first began studying how bacteria fight virus infections, she had no idea it ...

To compete at iGEM, a sort of science Olympics, teens at a Georgia high school set their sights on finding a better way to ...

Cleveland Clinic researchers have discovered they may be able to shut off the cholesterol gene. Mike Johnson scrambles to pass Pentagon bill as GOP ranks seethe ...

An experimental gene-editing treatment shows promise for permanently lowering levels of cholesterol and triglycerides, possibly helping cut the... CRISPR gene-editing works to reduce high cholesterol ...