The FDA has granted approval to a new gene therapy for a rare immune disorder, the maker of which is notably not a drug ...
The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...
Backed by Italy-based Fondazione Telethon ETS, Waskyra, for Wiskott-Aldrich syndrome, is the first gene therapy from a ...
Vertex Pharmaceuticals said on Saturday its gene therapy helped children aged between 5 and 11 years with sickle cell disease ...
Huntington’s disease is one of the cruelest genetic afflictions a family can endure. The condition, which affects around 41,000 Americans, is the result of an error ...
A three-year-old Oliver (Ollie) Chu has become the world’s first patient to receive a revolutionary stem cell gene therapy for Hunter syndrome. This rare, progressive, inherited disorder damages the ...
Nov 24 (Reuters) - (This Nov 24 story has been corrected to fix the pricing for Zolgensma to $2.5 million from $2.1 million in paragraph 4) The U.S. Food and Drug Administration has approved Novartis' ...
Mixed headlines have plagued the cell and gene therapy space of late. We believe that a renewed case of optimism is not only warranted but essential if these therapies are to reach their full ...
What does the U.S. government know about “unidentified aerial phenomena” (UAPs), aliens and an alleged global alien technology arms race? A brand-new documentary claims to have an answer: more than it ...
The topic of Alzheimer’s has been a personal issue for Chris Hemsworth and his family for some time. The Australian actor ...
Copyright 2025 The Associated Press. All Rights Reserved. Copyright 2025 The Associated Press. All Rights Reserved. The name and logo of Sarepta Therapeutics is ...
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