The FDA on Tuesday approved etuvetidigene autotemcel (Waskyra) as the first cell-based gene therapy for patients 6 months and ...

Three years after introducing Hemgenix, the first gene therapy for hemophilia B, CSL Behring has released long-term data ...

Novartis’ Itvisma wins FDA approval as the first gene replacement therapy for spinal muscular atrophy (SMA) patients age 2 ...

Kids and teenagers with spinal muscular atrophy had more mobility after receiving a single-dose gene replacement therapy, ...

Menopausal hormone therapy (MHT) does not raise breast cancer risk in women with breast cancer gene mutations, while estrogen only MHT leads to reduced risk.

Research by University of Sydney scientists has uncovered a mechanism that may explain why glioblastoma returns after ...

Pairing a drug that targets the PRDM9 gene with a cholesterol-lowering agent shrank brain tumors and improved survival in mice.

Tokenization is emerging as a cornerstone of modern data security, helping businesses separate the value of their data from ...

Scientists discovered that certain gene changes allow cells to function even when frataxin, the protein lost in Friedreich’s ...

A study by University of Sydney scientists has discovered why patients with glioblastoma often relapse, identifying a hidden ...

Menin inhibitors target the interaction between menin and the KMT2A complex, offering a breakthrough in treating acute ...

The status could support staged transitions to new manufacturing processes, potentially mitigating some risks of high-stakes ...