Scientists discovered that certain gene changes allow cells to function even when frataxin, the protein lost in Friedreich’s ...

The patchwork rollout of a gene therapy exposes weaknesses in the pricing and regulatory frameworks that determine who ...

To our immune system, a potentially lifesaving gene therapy can look a lot like a dangerous infection. That's because most ...

A laboratory study out of Roswell Park Comprehensive Cancer Center outlines a new way to boost the effectiveness of chimeric ...

Eli Lilly will not seek a broad FDA approval for a combination of the company’s oral SERD med Inluriyo and CDK4/6 inhibitor ...

The Muscular Dystrophy Association (MDA) recognizes the U.S. Food and Drug Administration (FDA) approval of Amgen’s UPLIZNA ® (inebilizumab-cdon) for the treatment of generalized myasthenia gravis ...

In the 21st century, oncology has achieved extraordinary progress. We can decode a tumor’s genome, tailor therapies to ...

Brent Saunders returned to Bausch + Lomb in 2023 to help address unmet needs in eye care, focusing on innovation and ...

In atopic dermatitis, the first interleukin-22 inhibitor to reach late clinical trials is showing uncommonly broad suppression of biomarkers associated with disease activity.

Only 6% of trials for FDA-approved drugs match America's diversity. Analysis reveals how trial location and design choices ...

For years, orange juice has been sold as a simple source of vitamin C, but new human data suggest that a morning glass may be ...