ORLANDO -- A gene therapy that could transform CAR T-cell treatment achieved rapid and potentially durable measurable ...

An experimental gene therapy treatment created at UCLA gave a "bubble girl" born with a rare genetic disorder a new life.

Dr. Teresa Blankmeyer Burke is spending the fall semester in Florianópolis, a city in southern Brazil, to study the ethics of ...

A cutting-edge therapy using base-edited immune cells is offering a major breakthrough for patients with one of the toughest ...

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...

FDA clears first gene therapy for rare disease; Roche’s breast cancer pill win; Women increasingly turn to GLP-1s.

The first-line standard of care for HR-positive/HER2-negative breast cancer is cyclin-dependent kinase (CDK)4/6 inhibitors ...

Abeona Therapeutics Inc. (Nasdaq: ABEO) today announced activation of The University of Texas Medical Branch (UTMB) in ...

They manage to slow down the progression of Huntington's disease using a gene therapy treatment called AMT 130.

At an FDA discussion of testosterone replacement therapy, a top official called for special health centers to address a ...

In today’s Pharmaceutical Executive Daily, new analysis outlines what it may truly cost to fix the biopharma ecosystem, the ...

A common cold was enough to kill Cora Oakley. Born in Morristown, New Jersey, with virtually no immune system, Cora was diagnosed with severe combined immunodeficiency, a rare genetic condition that ...