During this season of hope, columnist Robin Stemple shares his wishes for both the disability community and himself.

Experimental therapy deramiocel outperformed a placebo at improving measures of arm and heart health in people with DMD in a ...

A regimen of three immune-suppressing drugs may improve the effectiveness of gene therapy for people with DMD, research in ...

Columnist Shalom Lim attended a musical honoring healthcare professionals and, as someone with Duchenne MD, came away feeling ...

Upsher-Smith Laboratories launched DMD treatment Kymbee in the U.S., backed by a support program for patients.

Columnist Patrick Moeschen argues that we all should focus more on finding the right words to accurately describe living with chronic illness.

Columnist Betty Vertin is planning a holiday season this year that will let her sons with DMD better enjoy their time with family and friends.

With three sons with Duchenne MD, columnist Betty Vertin has little time for housework, making her regret not giving the other kids chores.

A Phase 1/2 clinical trial testing SRP-1003, a treatment for myotonic dystrophy type 1 (DM1), is progressing as planned and continues to enroll patients at higher doses. The Phase 1/2 study ...

What is Elevidys for Duchenne muscular dystrophy? Elevidys (delandistrogene moxeparvovec-rokl), previously known as SRP-9001, is a one-time gene therapy approved in the U.S. to treat patients with ...