Experimental therapy deramiocel outperformed a placebo at improving measures of arm and heart health in people with DMD in a ...
Columnist Patrick Moeschen argues that we all should focus more on finding the right words to accurately describe living with chronic illness.
Columnist Betty Vertin is planning a holiday season this year that will let her sons with DMD better enjoy their time with family and friends.
Upsher-Smith Laboratories launched DMD treatment Kymbee in the U.S., backed by a support program for patients.
Columnist Shalom Lim attended a musical honoring healthcare professionals and, as someone with Duchenne MD, came away feeling ...
A regimen of three immune-suppressing drugs may improve the effectiveness of gene therapy for people with DMD, research in ...
With three sons with Duchenne MD, columnist Betty Vertin has little time for housework, making her regret not giving the other kids chores.
Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...
A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.
When I was a young mom watching my oldest daughter, Lexi, move from upper elementary to middle school, I often felt heartbroken and helpless. She was an excellent student and friend at school, but ...